Our Research Focus
Krabbe Disease
Krabbe disease is a severe, inherited, neurological condition. It is part of a group of disorders known as leukodystrophies, which result from the loss of myelin in the nervous system.
Learn More About Krabbe Disease
Cystic Fibrosis
Cystic fibrosis is a severe genetic disease that causes lung infections and limits the ability to breathe over time and can keep the body from absorbing food.
Learn More About Cystic Fibrosis